CC BY-NC-ND 4.0 · Endosc Int Open 2024; 12(04): E629-E638
DOI: 10.1055/a-2251-3372
Original article

Efficacy and safety of a new low-volume PEG with citrate and simethicone bowel preparation for pediatric elective colonoscopy: Phase 3 RCT

Giusy Russo
1   Pediatric Gastroenterology and Liver Unit, Maternal and Child Health Department, Sapienza University of Rome, Rome, Italy (Ringgold ID: RIN9311)
,
Patrizia Alvisi
2   Department of Paediatrics, Ospedale Maggiore, Local Health Authority, Ospedale Maggiore di Bologna, Bologna, Italy
,
Claudio Romano
3   Pediatric Gastroenterology and Cystic Fibrosis Unit, Department of Human Pathology in Adulthood and Childhood "G. Barresi", University of Messina, Messina, Italy
,
Giulia Angelino
4   Digestive Endoscopy and Surgery Unit, Bambino Gesù Children's Hospital IRCCS, Rome, Rome, Italy
,
Julie Lemale
5   Department of Pediatric Nutrition and Gastroenterology, Armand-Trousseau Childrens Hospital, Paris, France (Ringgold ID: RIN36879)
,
Alain Lachaux
6   Department of Pediatric Gastroenterology, Hepatology and Nutrition, Children's Hospital of Lyon, BRON, France
,
Paolo Lionetti
7   Pediatric Gastroenterology and Nutrition Unit, Meyer Children's Hospital, Florence, Italy
,
Genevieve Veereman
8   Department of Pediatric Gastroenterology and Nutrition, University Hospital Brussels, Brussels, Belgium
,
Cosimo Ruggiero
1   Pediatric Gastroenterology and Liver Unit, Maternal and Child Health Department, Sapienza University of Rome, Rome, Italy (Ringgold ID: RIN9311)
,
Michela Padovani
9   Corporate R&D Department, Alfasigma SpA, Bologna, Italy (Ringgold ID: RIN9324)
,
Raffaella Tacchi
9   Corporate R&D Department, Alfasigma SpA, Bologna, Italy (Ringgold ID: RIN9324)
,
Fabio Cenci
9   Corporate R&D Department, Alfasigma SpA, Bologna, Italy (Ringgold ID: RIN9324)
,
Salvatore Cucchiara
1   Pediatric Gastroenterology and Liver Unit, Maternal and Child Health Department, Sapienza University of Rome, Rome, Italy (Ringgold ID: RIN9311)
,
Salvatore Oliva
1   Pediatric Gastroenterology and Liver Unit, Maternal and Child Health Department, Sapienza University of Rome, Rome, Italy (Ringgold ID: RIN9311)
› Author Affiliations
Supported by: Alfasigma SpA

Clinical Trial: Registration number (trial ID): NCT03106922, Trial registry: ClinicalTrials.gov (http://www.clinicaltrials.gov/), Type of Study: Prospective, multicenter, randomized, single-blind study

Abstract

Background and study aims Currently available polyethylene glycol (PEG)-based preparations continue to represent a challenge in children. The aim of this study was to compare the efficacy and safety of a new low-volume PEG preparation with a conventional PEG-electrolyte solution (PEG-ES) in children and adolescents.

Patients and methods This was a multicenter, randomized, observer-blind, parallel-group, phase 3 clinical trial, where patients were randomized between PMF104 (Clensia) and a conventional PEG-ES (Klean-Prep), and stratified by age stratum (2 to <6; 6 to < 12;12 to <18 years). The primary endpoint was to test the non-inferiority of PMF104 versus PEG-ES, in terms of colon cleansing. Safety, tolerability, acceptability, palatability, and compliance were also assessed. Efficacy endpoints were analyzed in the per protocol set (PPS) and full analysis set (FAS) and safety and tolerability endpoints in the safety set (SAF).

Results Of the 356 patients enrolled, 258 were included in the PPS, 346 in the FAS, and 351 in the SAF. Non-inferiority of PMF104 was confirmed for children aged > 6 years and for all age groups in PPS and FAS, respectively. Optimal compliance was reported more frequently in the PMF104 than in the PEG-ES group, in both PPS (86.1% vs. 68.4%) and FAS (82.9% vs. 65.3%).

Both preparations were equally safe and tolerable. Palatability and acceptability were considered better in the PMF104 group than in the PEG-ES group (27.1% vs. 15.3% and 15.3% vs. 3.5%, respectively).

Conclusions In children aged 6 to 17 years, the new low-volume product PMF104 is non-inferior to the reference PEG-ES in terms of bowel cleansing, safety, and tolerability, with slightly better results in compliance, palatability, and acceptability.

Supplementary Material



Publication History

Received: 07 November 2022

Accepted after revision: 17 January 2024

Accepted Manuscript online:
22 January 2024

Article published online:
26 April 2024

© 2024. The Author(s). This is an open access article published by Thieme under the terms of the Creative Commons Attribution-NonDerivative-NonCommercial-License, permitting copying and reproduction so long as the original work is given appropriate credit. Contents may not be used for commercial purposes, or adapted, remixed, transformed or built upon. (https://creativecommons.org/licenses/by-nc-nd/4.0/).

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